Discover how pediatric physiotherapy supports children's developmental milestones, helping build strength, coordination & confidence through intervention.

The Food and Drug Administration (FDA) has granted accelerated approval to Kebilidi™ (eladocagene exuparvovec-tneq) for the treatment of adult and pediatric patients with aromatic L-amino acid ...

The FDA has followed in the footsteps of its European counterparts and granted accelerated approval to PTC Therapeutics’ gene ...

Results from the study showed progressive and continued post-dose improvement in gross motor function and achievement of motor milestones in participants treated with BBP-812. Significant and ...